Slashdot is powered by your submissions, so send in your scoop

 



Forgot your password?
typodupeerror
×
Medicine Businesses The Almighty Buck

A Controversial Autism Treatment Is About To Become a Very Big Business (vice.com) 141

An anonymous reader quotes a report from Motherboard: At Duke University's Marcus Center for Cellular Cures, parents can enroll their children into a number of clinical trials that aim to study the effects of cells derived from umbilical cord blood on treating the effects of autism and brain injuries; adults can also participate in a trial testing whether cord blood can help them recover from ischemic strokes. And when parents can't get their children into any of these clinical trials, particularly for autism, they often opt for what's called the Expanded Access Program (EAP), in which they pay between $10,000 and $15,000 to get their kids a single infusion. All of the trials use products derived from human umbilical cord blood, which is a source of stem cells as well as other types of cells. The autism trials are using a type of immune cells called monocytes, according to Dr. Joanne Kurtzberg, a well-respected Duke professor who's conducting clinical trials into whether cord blood can help with autism, and who has been researching stem cells since the early '90s. (On ClinicalTrials.gov, however, these trials are listed as using mesenchymal stromal cells, which are a completely different type of cord blood cell.)

Now, a for-profit company called Cryo-Cell International with ties to Duke researchers has indicated that it plans to open clinics promoting these treatments, under a licensing agreement with the renowned North Carolina university. In their investor presentation, Cryo-Cell said they plan to become "an autonomous, vertically integrated cellular therapy company that will treat patients." Duke and Cryo-Cell's rush to monetize a procedure before it's shown to have solid benefits has created concern, though, across the community of scientists, clinicians, and medical ethicists who study autism treatments. The hope is that these cord blood infusions can improve some autism symptoms, like socialization and language, or decrease the inflammation that some parents and clinicians think might exacerbate autism symptoms. Early study results, however, haven't been very promising.

A large randomized clinical trial, the results of which were released in May 2020, showed that a single infusion of cord blood was not, in the words of the researchers, "associated with improved socialization skills or reduced autism symptoms." This is why Duke's latest move comes as such a surprise: The university and Cryo-Cell have told investors that they're planning to open a series of "infusion centers." At these clinics, Cryo-Cell will use Duke's technology and methods to offer cord blood treatments for $15,000 per infusion. In an exuberant presentation for investors (PDF), Cryo-Cell said it estimates an annual revenue of $24 million per clinic; it hasn't disclosed how many clinics it plans to open. At least one will reportedly open in Durham, North Carolina. The move follows a June 2020 announcement that Cryo-Cell had entered into an exclusive patent-option agreement with Duke, allowing it to manufacture and sell products based on patents from Dr. Joanne Kurtzberg.

This discussion has been archived. No new comments can be posted.

A Controversial Autism Treatment Is About To Become a Very Big Business

Comments Filter:
  • by Kaenneth ( 82978 ) on Wednesday October 06, 2021 @10:43PM (#61868197) Journal

    What's the theoretical mechanism of action?

  • by khchung ( 462899 ) on Wednesday October 06, 2021 @10:57PM (#61868229) Journal

    Not very surprising when you have a huge for-profit health care system. You would be naive to think this is simply an "expensive treatment for X" which could happen just anywhere in the world.

    Think Silicon Valley, could internet giants like Google happen just anywhere in the world? No, Silicon Valley is unique in the way it has the right VC money, the right tech people, and the right startup culture. These things emerge through time in the right environment and cannot be mandated, else we would have seen SV replicated everywhere in the world.

    It is the same with big pharma. After decades of for-profit health care, the entire ecosystem of money, people and culture now exists to seek profit from anything people would buy. Pharma making more money does not necessarily means better health for more people, it could also mean treatment for any sickness, real or perceived, that people are willing to pay. It is especially despicable to target children because most parents would pay almost anything for their children, it is a direct exploitation of human nature for profit.

    Perhaps Americans should reflect if this is the direction they would like to keep going.

    • by Luckyo ( 1726890 ) on Wednesday October 06, 2021 @11:55PM (#61868289)

      This isn't about healthcare system. This is about the horror show that is a family with an autistic child. It is a genuine deep and painful tragedy that just keeps going and going for as long as parents are alive.

      There's a horrific truth that is understood by parents of a low functioning autistic child. "My child will survive for as long as I live". Because that's what often happens. And every day there is indeed survival rather than living. It's an utter desperation for every hour of every day of every week of every month of every year, until the end of your natural life.

      So it's no wonder that any fix, no matter how unlikely is going to have many takers, as long as its even remotely affordable.

      Problems with cost of US medical system are mainly related to curable/treatable illnesses that cost far more than it should to get treated. It's not so much with incurable/untreatable, difficult to manage lifetime disabilities, because every systems has significant problems handling those.

      • by hey! ( 33014 ) on Thursday October 07, 2021 @12:23AM (#61868335) Homepage Journal

        No, since the treatment has not been shown to be effective (in fact it looks like it's not effective), it absolutely *is* about the healthcare system exploiting the very reasonable concerns of parents for profit rather than their benefit.

        • Re: (Score:2, Offtopic)

          by Luckyo ( 1726890 )

          Fundamental assumption that must be true for this to be about "US healthcare system": This sort of thing doesn't happen in other healthcare systems.

          Meanwhile in Germany, where homeopathic products is sold in apothecaries next to actual medicine. Damn, US medical system is in Germany. Meanwhile in PRC, where Traditional Chinese Medicine is held in higher regard and more available than actual medicine. Damn, US medical system is in Germany. Meanwhile in South Africa, where Zulu Witchcraft is considered a viab

          • Fundamental assumption that must be true for this to be about "US healthcare system": This sort of thing doesn't happen in other healthcare systems.

            Meanwhile in Germany, where homeopathic products is sold in apothecaries next to actual medicine.

            Meanwhile in PRC, where Traditional Chinese Medicine is held in higher regard and more available than actual medicine.

            Meanwhile in South Africa, where Zulu Witchcraft is considered a viable alternative to actual medicine.

            How many of your examples cost 10,000 -15,000 $US a pop?

            • by Luckyo ( 1726890 )

              When adjusted for purchasing power? All of them.

            • Homeopathetic "cures" are fairly cheap. But still the most expensive way to buy sugar.

          • by piojo ( 995934 )

            One nit to pick: Traditional Chinese medicine is not in the same category as homeopathy, since many plants are pharmacologically active. They're both dogmas, but one is based on magic and the other is based on observations. Though I won't deny TCM contains a lot of BS and/or treatments that haven't been proven effective.

            • Ok, not all of TCM is bullshit. But can we at least agree that stuff like Rhino horn is bunk?

              By that logic, I can as well start to trust my wise woman with the various plants cut at the right moon phase again. Yes, some of their stuff has medical properties, but the whole mumbo jumbo around it is bullshit, and you're still better off with traditional actual medicine.

              • By that logic, I can as well start to trust my wise woman with the various plants cut at the right moon phase again.

                At the time when allopathic medicine deliberately diverged from naturopathic medicine the two were about equally effective, and the common saying was that with naturopathic medicine you died of the disease while with allopathic medicine you died from the cure. If we had applied as much science to naturopathic medicine as we have to allopathic, one wonders what the results might have been. Probably we'd still have been screwed because we'd still have been driving plants to extinction left and right before we

                • You'll find that a lot of the cures we have today are derivatives of various natural compounds. Mostly because it's pretty expensive to fully synthesize complex molecules.

              • by piojo ( 995934 )

                Yeah, that's exactly what I'm saying. The village wise woman is more trustworthy than literal magic. And while rhino horns and tiger penises make the news, typically it's just foul tasting herbs, mixed in a combination intended to target the symptoms.

            • by Luckyo ( 1726890 )

              You seem to think that homeopathy is not "based on observations", as that is the distinction you're drawing.

              You're wrong. It's just that just like with TCM and other "traditional medicines", observations are typically subjective, faulty and often downright falsified.

      • As a parent of an Autistic son I totally reject you characterization of autism.
        Your description does not agree with my life nor does it reflect the situation me and my wife are seeing around us (and my wife is treating ASS professionally)

        Yes an person with ASS requires attention for his sensitivities each and every day. Yes ASS persons have a normal life expectancy. Yes getting the ASS diagnosis for your child does feel like a life sentence when you first hear it.

        But describing it as a tragedy and basically

        • by Luckyo ( 1726890 )

          >But describing it as a tragedy and basically stating that in order to find a 'cure' anything goes? No. I reject that line of reasoning entirely.

          Do what you feel is necessary to survive your personal circumstances. But don't you dare minimize it, because for every one of you who can draw sufficient strength to handle his personal tragedy, there are a dosen of parents that are at the end of their rope. Some of them literally.

          • .. there are a dozens of parents that are at the end of their rope. Some of them literally.

            I. Know.
            Don't you think I have been 'at the end of my rope' numerous times?
            But so are parents of children with the down syndrome, paralyzed, with a CVA...

            The point is: how can we help a family in such a situation? I would like to plead for compassion, helping in small ways and providing the best medical and social care possible.

            For me, commercializing a very expensive, unproven treatment and pushing this to strained parents is not helping. It is abusing the desperation of people in need for commercial gain.

            • by Luckyo ( 1726890 )

              >The point is: how can we help a family in such a situation?

              The most typical kind of help is where you have an organisation that will have professionals and volunteers assisting them take care of severely autistic children for a while, to give parents time maybe once a week, maybe once a month to just go and be on their own. Have reprieve from that constant terror at home that something will set the severely autistic teenager or adult off. This requires significant amount of resources, which society will

      • by nagora ( 177841 )

        This isn't about healthcare system. This is about the horror show that is a family with an autistic child. It is a genuine deep and painful tragedy that just keeps going and going for as long as parents are alive.

        That's exactly the problem with a private healthcare system - a horror like this is a perfect way to extort money from people in a way that salaried healthcare workers would not be/are not motivated to do.

        Any time there's some case of a child with a rare untreatable disease, private healthcare crawls out of the woodwork to offer expensive useless regimes of drugs, radiation, or just plain vapourware, some of it quite invasive and painful.

        • by Luckyo ( 1726890 )

          Ah yes, the "private medical system". Like the traditional Chinese medicine offered as the main public medical system offering in China. Like the homeopathy offered as a part of public medical system in Germany.

          It's better to stay silent and let others think you an idiot, than open your mouth and remove all doubt.

          • by nagora ( 177841 )

            Ah yes, the "private medical system". Like the traditional Chinese medicine offered as the main public medical system offering in China. Like the homeopathy offered as a part of public medical system in Germany.

            It's better to stay silent and let others think you an idiot, than open your mouth and remove all doubt.

            Ooooh, you cherry-picked two examples - one of which is a very very minor player - to balance out the whole of private medical healthcare's routine and enormous industrialised blackmail system.

            How very clever of you.

          • It's better to stay silent and let others think you an idiot, than open your mouth and remove all doubt.

            Never thought you'd be so self aware.

    • I can't exactly put my finger on why, but it just doesn't feel right when companies charge for medicine what the market will bear.

      • Yes it cannot be denied that healthcare based on ability to pay is fundamentally amoral. A frequent retort by those that oppose single payor universal healthcare is that it would lead to rationing of healthcare. The comedy is that we're already rationing healthcare, it's just rationed based on how much you can pay. And we only have as many healthcare workers, facilities and services as the group of fortunates that can pay is able to support and they're concentrated in areas with the most able to pay.

        Whil

    • No, Silicon Valley is unique in the way it has the right VC money, the right tech people, and the right startup culture.

      ... and the fact that non-compete agreements are not valid.

    • News flash: Most American people don't like the direction we're going when it comes to healthcare. The only people happy with it are those that exploit it to rake in piles of cash, and the government officials that get massive kickbacks for keeping the system running the way it is. Most of us want real change. Instead we get bullshit money grabs like the Affordable Care Act, which has priced out a large chunk of the middle class from even being able to afford the shit-show insurance we used to be able to

    • by pjt33 ( 739471 )

      Think Silicon Valley, could internet giants like Google happen just anywhere in the world? No, Silicon Valley is unique in the way it has the right VC money, the right tech people, and the right startup culture. These things emerge through time in the right environment and cannot be mandated, else we would have seen SV replicated everywhere in the world.

      I know this is a bit of a side-discussion, and you may have meant that as a throwaway remark, but I think that the reason that there isn't really a European

  • Can I get it in a smoothie with kale and acai berries?
  • by h33t l4x0r ( 4107715 ) on Wednesday October 06, 2021 @11:16PM (#61868255)
    Hell I can get you a cord by 3 o'clock this afternoon. With nail polish.
  • Likely any deep scientific field or company is full of autistic people, likely the ones that are able to obsess for long enough to achieve results. No doubt also in their own organization.

    Hopefully they won't hesitate to inject it into their own scientists first. Especially the autistic ones behind the research itself.

    • by vbdasc ( 146051 )

      Likely any deep scientific field or company is full of autistic people, likely the ones that are able to obsess for long enough to achieve results. No doubt also in their own organization.

      Hopefully they won't hesitate to inject it into their own scientists first. Especially the autistic ones behind the research itself.

      The autistic people you mention are high-functioning, while this whole enterprise is about milking parents of LOW-FUNCTIONING autistic kids. There is a difference between these groups, you know.

      With all that said, it's sad that a respected research center like Duke got involved in a scheme that to me personally at least, looks like snake oil peddling and shameless quackery. Money can corrupt everyone after all, I guess.

  • My bold prediction is that this will get shut down before they even open for business.

  • Before even one for-profit clinic opens, every taxpayer dollar that went into the development of the procedure should be recovered from these creeps in blood, at a penny a pint.

  • https://medicalxpress.com/news... [medicalxpress.com] "A parent-led intervention that supports the social development of babies displaying early signs of autism has significantly reduced the likelihood of an autism diagnosis being made in early childhood,"

    So in other words: If you socialize your babies properly, they're a whole lot less likely to end up being unable to socially interact later.

    Sort of like if you buy a puppy and don't socialize it around other dogs while it's growing up, it's going to be an unstable neuro
    • So in other words: If you socialize your babies properly, they're a whole lot less likely to end up being unable to socially interact later. Sort of like if you buy a puppy and don't socialize it around other dogs while it's growing up, it's going to be an unstable neurotic wreck around them as an adult.

      Taking this simplistic view of what is said in the article at face value, we should see a dramatic rise in autism diagnoses over the coming years due to a long period of COVID lockdown, where babies and toddlers were unable to attend playgroups and activities that would usually have been available to them, nor in some countries, even visit close relatives for an extended period of time.

      Of course, that's not what the article said at all, but you should be able to prove your own hypothesis with actual dat

  • As the parent of an autistic, this sounds like a load of rubbish to me. We'll see I guess, but right now I don't believe it.

  • Stamina therapy? (Score:4, Informative)

    by apetrelli ( 1308945 ) on Thursday October 07, 2021 @04:43AM (#61868621)

    In Italy a similar treatment ended up with being declared as a fraud:
    https://en.wikipedia.org/wiki/... [wikipedia.org]

    • In Italy a similar treatment ended up with being declared as a fraud:
      https://en.wikipedia.org/wiki/... [wikipedia.org]

      However, that wiki article for the Stamina therapy used in Italy says: "It was found that the cell preparations did not contain any relevant quantities of mesenchymal stem cells". So the stamina therapy didn't actually contain what it was supposed to contain.

      • In Italy a similar treatment ended up with being declared as a fraud:
        https://en.wikipedia.org/wiki/... [wikipedia.org]

        However, that wiki article for the Stamina therapy used in Italy says: "It was found that the cell preparations did not contain any relevant quantities of mesenchymal stem cells". So the stamina therapy didn't actually contain what it was supposed to contain.

        I bet that it will end up the same way. The Stamina therapy also has been associated with the hospital of Brescia. The theorist was not, indeed, a doctor, but he graduated in journalism. So in the North Carolina case it is much different but...
        Don't you think that they will take this umbilical cord not to cure people or do real research, but to sell it, a thing that cannot be done? In Italy umbilical cord is donated, not sold, voluntarily and only in certain hospitals.
        So I think that they may end up in sell

  • Maybe this is why so many people distrust medicine.
  • The sad part is that the parents of children with severe cases of autism will pay almost anything for even a shred of hope that it will improve their child's quality of life. They are desperate. That is why many fell for the line of hokum that vaccines were somehow to blame for the condition. So while I'm extremely empathetic to the parents who are left grasping at any shred of assistance, I find it contemptible that there are people out there that want to take advantage of that desperation for profit.

  • ... that there will be a vaccine for Slashdot soon?

  • I am just a layperson interested in the gut microbiome, and have seen very interesting connections between it and autism. I just encountered this article (https://www.jillcarnahan.com/2021/03/30/understanding-the-link-between-autism-and-the-microbiome/) which not only describes the altered gut microbiome of people with autism, but also how the microbiome of mothers play a role in shaping their children's neurology and microbiome.

    There is much more to be understood, but it would seem that certain bacteria
  • for "Total shit, but we want to appear 'fair and balanced and neutral' even when the case is clear-cut.".

Keep up the good work! But please don't ask me to help.

Working...